Niemann-Pick Disease Type C from Bench to Bedside
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Intrathecal 2-hydroxypropyl-�-cyclodextrin Decreases Neurological Disease Progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1-2 trial
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The Neurobiology, Diagnosis, and Treatment of Narcolepsy
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The Narcolpetic Syndrome
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